: the insertion of usually genetically altered genes into cells especially to replace defective genes in the treatment of genetic disorders or to provide a specialized disease-fighting function
gene therapistnoun
Example Sentences
advances in the science of gene therapy
Recent Examples on the WebElevateBio incubates, launches, and operates biotech companies focused on cell and gene therapy. Anissa Gardizy, BostonGlobe.com, 4 Aug. 2022 But one major problem is that the drug manufacturing process is antiquated in many facilities, said Kwok Pang, an executive at the cell and gene therapy biotech Autolomous. Angus Chen, STAT, 2 June 2022 Two children who received Zolgensma, Novartis AG’s gene therapy for a rare condition called spinal muscular atrophy, died from liver complications. Angelica Peebles, Bloomberg.com, 11 Aug. 2022 Twenty-three years ago, the field of gene therapy was bursting with the promise of breakthrough treatments. Eric B. Kmiec, STAT, 13 July 2022 Fortunately, the experimental gene therapy seemed to work; Janz began to feel better. Sarah Zhang, The Atlantic, 22 June 2022 Kathy Wilkes, 71, of Ormond Beach, Florida, received an experimental gene therapy in 2021 to fight her advanced pancreatic cancer. Reynolds Lewis, NBC News, 2 June 2022 At the same time, its stock dropped 25.9% after disclosing new safety issues with an experimental gene therapy under development to treat cerebral adrenoleukodystrophy, a rare genetic condition. Ed Silverman, STAT, 12 Aug. 2021 The agency has promised to render a final decision on Bluebird’s gene therapy, called beti-cel, by Aug. 19. Damian Garde, STAT, 13 June 2022 See More